modeling of GM1 gangliosidosis using iPSC-derived cellular and organoid CNS models
In: Molecular Genetics and Metabolism, Jg. 138 (2023), Heft 2, S. 107309
academicJournal
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modeling of GM1 gangliosidosis using iPSC-derived cellular and organoid CNS models
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Autor/in / Beteiligte Person: | Schmitt, Christopher E. ; Lee, Grace S. ; Onguka, Ouma ; Wong, Victoria ; Del Greco, Elizabeth ; Sedighi, Faezeh ; Reddy, Charu ; Santosh, Swetha ; Akinkugbe, Oluwayomi ; Artz, Jacob ; Kruse, Nikki ; Chng, Chinping ; Hallows, William C. ; Chen, Joseph C. ; Akeefe, Hassibullah ; Silverman, Adam P. ; Huisman, Gjalt |
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Zeitschrift: | Molecular Genetics and Metabolism, Jg. 138 (2023), Heft 2, S. 107309 |
Veröffentlichung: | Elsevier BV, 2023 |
Medientyp: | academicJournal |
ISSN: | 1096-7192 |
DOI: | 10.1016/j.ymgme.2022.107309 |
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