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Safety and Long-Term Efficacy of AAV4 Gene Therapy in Patients with RPE65 Leber Congenital AmaurosisIn: Molecular Therapy ; volume 26, issue 1, page 256-268 ; ISSN 1525-0016, 2018academicJournalZugriff:
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In: Molecular Therapy ; volume 25, issue 2, page 547-559 ; ISSN 1525-0016, 2017academicJournalZugriff:
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In: Molecular Therapy ; volume 24, issue 8, page 1470-1477 ; ISSN 1525-0016, 2016academicJournalZugriff:
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In: Molecular Therapy ; volume 24, page S275-S276 ; ISSN 1525-0016, 2016academicJournalZugriff:
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In: Molecular Therapy ; volume 24, page S200 ; ISSN 1525-0016, 2016academicJournalZugriff:
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In: Molecular Therapy ; volume 23, page S9 ; ISSN 1525-0016, 2015academicJournalZugriff:
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In: Molecular Therapy ; volume 22, issue 11, page 1923-1935 ; ISSN 1525-0016, 2014academicJournalZugriff:
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In: Molecular Therapy ; volume 22, issue 9, page 1605-1613 ; ISSN 1525-0016, 2014academicJournalZugriff:
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In: Molecular Therapy ; volume 18, issue 1, page 151-160 ; ISSN 1525-0016, 2010academicJournalZugriff:
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In: Molecular Therapy ; volume 17, issue 3, page 472-479 ; ISSN 1525-0016, 2009academicJournalZugriff:
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In: PLoS ONE, Jg. 14 (2019-10-10), Heft 10, S. 1-15Online academicJournalZugriff:
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In: PLoS ONE, Jg. 14 (2019-09-16), Heft 9, S. 1-11Online academicJournalZugriff: